Natural History of Atypical Morquio A Disease
NCT03204370
·
clinicaltrials.gov ↗
COMPLETED
Status
7
Enrollment
OTHER
Sponsor class
Conditions
Mucopolysaccharidosis IV A
Interventions
DRUG:
Elosulfase Alfa 1 MG/ML Intravenous Solution [VIMIZIM]
Sponsor
GOIZET
Collaborators
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