Farber Disease Natural History Study
Conditions
- Farber Disease
- Farber's Disease
- Farber Lipogranulomatosis
- Acid Ceramidase Deficiency
- Ceramidase Deficiency
- N-Laurylsphingosine Deacylase Deficiency
- ASAH1 Mutation
Sponsor
Sumitomo Pharma Switzerland GmbH