Strimvelis Registry Study to Follow-up Patients With Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID)
NCT03478670
·
clinicaltrials.gov ↗
ENROLLING_BY_INVITATION
Status
50
Enrollment
OTHER
Sponsor class
Conditions
Immunologic Deficiency Syndromes
Interventions
GENETIC:
Strimvelis
Sponsor
Fondazione Telethon