Lentiviral Gene Therapy for X-linked Severe Combined Immunodeficiency

NCT03601286 · clinicaltrials.gov ↗

PHASE1

Phase

RECRUITING

Status

5

Enrollment

OTHER

Sponsor class

Conditions

Severe Combined Immunodeficiency, X-Linked

Interventions

DRUG: Lentiviral vector transduced CD34+ cells

Sponsor

Great Ormond Street Hospital for Children NHS Foundation Trust