Use of Phenylbutyrate Therapy for Patients With Pyruvate Dehydrogenase Complex Deficiency.
NCT03734263
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
1
Enrollment
OTHER
Sponsor class
Conditions
Pyruvate Dehydrogenase Complex Deficiency
Interventions
DRUG:
sodium phenylbutyrate
Sponsor
Fondazione Telethon