Effects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD)

NCT03822013 · clinicaltrials.gov ↗

PHASE3

Phase

TERMINATED

Status

30

Enrollment

OTHER

Sponsor class

Stopped The number of controls was insufficient compared to case.

Conditions

GM2 Gangliosidosis
Supportive Care

Interventions

DRUG: Miglustat

Sponsor

Tehran University of Medical Sciences

Collaborators

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