Transcriptome and Metabolic Analyses of CHAPLE Disease
Conditions
- CD55 - Cluster of Differentiation Antigen 55 Deficiency
- Primary Intestinal Lymphangiectasis
- Protein-Losing Enteropathies
- Complement Regulatory Factor Defect
Interventions
- DRUG: Eculizumab Injection
Sponsor
Marmara University
Collaborators