Rescue of Infants With MCT8 Deficiency
NCT04143295
·
clinicaltrials.gov ↗
AVAILABLE
Status
OTHER
Sponsor class
Conditions
Mct8 (Slc16A2)-Specific Thyroid Hormone Cell Transporter Deficiency
Interventions
DRUG:
Diiodothyropropionic acid (DITPA)
Sponsor
Roy E. Weiss, M.D.