Low Dose Treosulfan Based Conditioning Regimen in HSCT for Nijmegen Breakage Syndrome
NCT04400045
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clinicaltrials.gov ↗
PHASE2
Phase
UNKNOWN
Status
10
Enrollment
OTHER
Sponsor class
Conditions
Nijmegen Breakage Syndrome
Interventions
DRUG:
Treosulfan
Sponsor
Federal Research Institute of Pediatric Hematology, Oncology and Immunology