Study of the Functional Effects of Nusinersen in 5q-spinal Muscular Amyotrophy Adults (SMA Type 2 or 3 Forms)

NCT04576494 · clinicaltrials.gov ↗

NA

Phase

COMPLETED

Status

4

Enrollment

OTHER

Sponsor class

Conditions

Spinal Muscular Atrophy

Interventions

OTHER: Monthly assessments of functional motor abilities by a trained therapist
DRUG: Nusinersen

Sponsor

CHU de Reims