Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy
NCT04959890
·
clinicaltrials.gov ↗
UNKNOWN
Status
15
Enrollment
OTHER
Sponsor class
Conditions
Severe Combined Immunodeficiency Due to ADA Deficiency
Interventions
GENETIC:
Strimvelis
Sponsor
Fondazione Telethon