NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Occipital Horn Syndrome
NCT04977388
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
3
Enrollment
OTHER
Sponsor class
Conditions
Menkes Disease
Occipital Horn Syndrome
Interventions
DRUG:
Droxidopa
OTHER:
Placebo
Sponsor
Stephen G. Kaler, MD