A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C

NCT05163288 · clinicaltrials.gov ↗

PHASE3

Phase

RECRUITING

Status

53

Enrollment

INDUSTRY

Sponsor class

Conditions

Niemann-Pick Disease, Type C

Interventions

DRUG: N-Acetyl-L-Leucine
OTHER: Placebo

Sponsor

IntraBio Inc