ATA-100 (Formerly GNT0006) Gene Therapy Trial in Patients With LGMDR9
NCT05224505
·
clinicaltrials.gov ↗
PHASE1
Phase
ACTIVE_NOT_RECRUITING
Status
6
Enrollment
INDUSTRY
Sponsor class
Conditions
LGMDR9
Interventions
BIOLOGICAL:
ATA-100 (AAV9 encoding FKRP gene)
Sponsor
Atamyo Therapeutics