Gene Therapy Study for Children With CLN5 Batten Disease

NCT05228145 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

ACTIVE_NOT_RECRUITING

Status

6

Enrollment

INDUSTRY

Sponsor class

Conditions

Neuronal Ceroid Lipofuscinosis CLN5

Interventions

GENETIC: NGN-101

Sponsor

Neurogene Inc.