Phase 1/2 Study of AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD)
Conditions
- FSHD
- FSHD1
- FSHD2
- FMD
- FMD2
- Fascioscapulohumeral Muscular Dystrophy
- Fascioscapulohumeral Muscular Dystrophy Type 1
- Fascioscapulohumeral Muscular Dystrophy Type 2
- Dystrophies, Facioscapulohumeral Muscular
- Dystrophy, Facioscapulohumeral Muscular
- Facioscapulohumeral Muscular Dystrophy 1
- Facioscapulohumeral Muscular Dystrophy 2
- Facio-Scapulo-Humeral Dystrophy
- Atrophy, Facioscapulohumeral
- Atrophies, Facioscapulohumeral
- Facioscapulohumeral Atrophy
- Muscular Dystrophies
- Muscular Dystrophy, Facioscapulohumeral
- FSH Muscular Dystrophy
- Landouzy Dejerine Dystrophy
- Landouzy-Dejerine Muscular Dystrophy
- Dystrophies, Landouzy-Dejerine
- Dystrophy, Landouzy-Dejerine
- Landouzy-Dejerine Syndrome
- Muscular Dystrophy, Landouzy Dejerine
- Progressive Muscular Dystrophy
- FSH
Interventions
- DRUG: AOC 1020
- DRUG: Placebo
Sponsor
Avidity Biosciences, Inc.