An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.

NCT05765981 · clinicaltrials.gov ↗
EARLY_PHASE1
Phase
RECRUITING
Status
6
Enrollment
OTHER
Sponsor class

Conditions

Interventions

Sponsor

Shanghai Jiao Tong University School of Medicine

Collaborators