WiTNNess - TNNT1 Myopathy Natural History Study
Conditions
- TNNT1-associated Myopathy
- Infantile-onset Nemaline Rod Myopathy
- Myopathies, Nemaline
- Myopathy
- Myopathy, Rod
- Myopathy; Hereditary
- Amish Nemaline Myopathy
- Nemaline Myopathy 5
- NEM5
- Genetic Muscle Disease
- Recessive Hereditary Disorder (Autosomal)
- ANM
Sponsor
Clinic for Special Children