A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of JWK008 in Patients With Mucopolysaccharidosis Type I

NCT06519552 · clinicaltrials.gov ↗

PHASE1

Phase

RECRUITING

Status

6

Enrollment

OTHER

Sponsor class

Conditions

Mucopolysaccharidosis Type I

Interventions

GENETIC: JWK008 Single intravenous infusion administration

Sponsor

West China Hospital