Gene Therapy for Alpha 1- Antitrypsin Deficiency
NCT06996756
·
clinicaltrials.gov ↗
PHASE1
Phase
RECRUITING
Status
16
Enrollment
OTHER
Sponsor class
Conditions
Alpha 1-Antitrypsin Deficiency
Interventions
BIOLOGICAL:
AAV8hAAT(AVL)
Sponsor
Weill Medical College of Cornell University
Collaborators
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