A Single Patient Study of Sapropterin for Multisystem Smooth Muscle Dysfunction Syndrome
NCT07574034
·
clinicaltrials.gov ↗
NA
Phase
NOT_YET_RECRUITING
Status
1
Enrollment
OTHER
Sponsor class
Conditions
Multisystemic Smooth Muscle Dysfunction Syndrome
Interventions
DRUG:
Kuvan (Sapropterine)
Sponsor
Gregor Andelfinger